Smart4fabry / News (Page 2)


The project was present in Austria for the Rare Diseases day 2019. The presentation of the Smart4Fabry Project and the technology DELOS-SUSP was presented by Johanna and Santi Sala (respectively) in the frame of the “First Austrian Microfluidics Initiative Symposium” hold the 28th February in Viena. In this Symposium organized by TUWien, TUGraz, Univ. Salzburg and BioNanoNet, a specific session with title “Rare Disease Day 2019” was scheduled. In this session three presentations were hold: Smart4Fabry project, Nanomol Technologies and its DELOS Susp technology and the H2020-MSCA-RISE-2017 “CISTEM” project.


Smart4Fabry partners from CIBER-VHIR, led by Dr. Ibane Abasolo, had a relevant presence at WORLDSymposium, held in Orlando, Florida, 4-8 February 2019. WORLD (We are Organizing Research on Lysosomal Diseases) Symposium is one of the most important events related to Lysososomal Diseases, like Fabry, at an international level. The goal of WORLDSymposium is to provide an interdisciplinary forum to explore and discuss specific areas of interest, research and clinical applicability related to lysosomal diseases. Each year, WORLDSymposium hosts a scientific meeting presenting the latest information from basic science, translational research, and clinical trials for lysosomal diseases. Our approach for an innovative treatment was presented as an oral communication and as a poster, increasing impact and visibility. It is worthy to mention that it was the only communication related to the application of nanomedicine to lysosomal storage diseases, showing the high innovation potential that Smart4Fabry posses.

Hospital Vall D´Hebron in collaboration with the H2020 funded Smart 4 Fabry project celebrated a seminar on Lisosomal Disorders, with a special focus on Fabry Disease.

Researchers and clinicians working in the field of lysosomal disorders had the opportunity to put in common the most recent advances in the diagnosis, pathophysiology and management of lysosomal storage disorders in general and of Fabry Disease in particular. During the seminar celebrated in Barcelona on November 19th, patients also had the chance to discuss with administrators and professionals about their expectations and demands, as well as their the need for collaborative actions aiming at designing plans for early diagnosis and easy access to the most suitable therapies.

Vall d’hebron Seminar – Lysosomal Disorders: focus on Fabry Disease

Genetic deficiencies of lysosomal components, most commonly enzymes, are known as “lysosomal storage disorders” (LSDs) and lead to lysosomal dysfunction, broadly affecting peripheral organs and the central nervous system, debilitating patients and frequently causing fatality. This seminar will update clinicians and researchers on most recent advances in diagnosis, pathophysiology and management of Fabry disease as well as in emerging therapies in the treatment of LSD. This seminar is supported by Smart4Fabry project.

Scientific Program

Smart4Fabry present at Clinam 2018 Summit

The CLINAM Summit is a globally unique event that brings together all stakeholders in nanomedicine, targeted medicine and precision medicine. Santi Sala, from Nanomol Technologies has participated into the session Presentations on Nanoparticles – Analytics, Methods and Technologies by presenting the work Technology platform for the production of lipid-based nanovesicles as new nanomedicines. By this presentation he has described latest developments related to our Horizon 2020 project “Smart-4-Fabry” – Smart multifunctional GLA-nanoformulation for Fabry disease.

Smart4Fabry presented at the Joint Japan-Spain Symposium on Medical Research

This event was held in Madrid on the 7th of November, in order to celebrate the 150th Anniversary of Japan-Spain Diplomatic Relations. Two key topic were innovation in rare diseases and nanomedicine. Enara Herran, from Biopraxis, presented several of Biopraxis R&D projects in these fields, highlighting Smart4Fabry as a clear example of how both Topics can be successfully combined. Japanese and Spanish high-level researchers, authorities, policy makers and representatives from biotech and health industries composed the audience.


A joint work elaborated by Smart4fFabry project partners Bionanonet, Joanneum Research and CIBER “Safe-by-design nanocarrier development – OFM to investigate blood-brain barrier crossing” was awarded the EUFEPS WIPS Award at the European Federation for Pharmaceutical Sciences 2018 Conference held in Athens (24-26 May 2018).

This award, Woman in Pharmaceutical Sciences Platform (WIPS), is intended to support women PhD students and post-doctoral researchers by facilitating their travels and participation in symposia and recognizes the excellent work presented by Christa Schimpel and Susanne Resch in the framework of Smart4Fabry.


SMART4FABRY project was presented to a wide, relevant audience at the last annual event of the European Technology Platform for Nanomedicine (ETPN) that was held in Berlin last May (28-30 May 2018).

ETPN annual event is the right place to discover, to network, to showcase, to design new projects, to brainstorm about the industrial expansion of Nanomedicine, all in a relaxed and friendly atmosphere. The audience included industry, researchers, healthcare providers, decision makers and European Commission representatives.

We introduced the overall technology platform that sustains Smart4Fabry as an opportunity for other rare diseases, to increase overall impact and offer potential treatments to unmet medical needs.

Smart4Fabry at Post WS RAREVIEW Symposium in Madrid

“POST-WS RAREVIEW, Innovation in lysosomal storage diseases” is the name of a Conference held in Madrid in April 2018. This meeting has joined more than 100 specialists from different clinical fields focused in lysosomal storage diseases, together with relevant stakeholders from the Pharmaceutical Industry. This forum mirrors, at a Spanish level, the 12th World Symposium Research for Lysosomal Diseases.
Smart4Fabry was represented by our Project Coordinator, Dr. Nora Ventosa, Dr Elisabet Gonzalez from CIBER/CSIC ICMAB and Dr Ibane Abasolo from CIBER/VHIR. This presence has been possible due to the cooperation established with CIBER-RER; a research network specialized in rare diseases. This meeting has been an excellent opportunity to introduce our project to clinicians and industrial partners, opening pathways for scientific collaboration and potential exploitation agreements.

S4F at 12th International Symposium on Supercritical Fluids 2018

The 12th International Symposium on Supercritical Fluids 2018 (ISSF 2018) was held in Antibes, France, at the end of April 2018. This Conference was focused on the most recent scientific and technological development.
A large place was proposed to case studies showing the ways taken to transform laboratory experiments into manufacturing innovative products in all types of industrial applications. Smart4Fabry was presented trough a lecture given by our PC Dr.
Nora Ventosa and this was an excellent opportunity to discuss technical solution with the compressed fluids community and the industrial equipment industry stakeholders.