Smart 4 Fabry 

Quality control, development, construction,
provide and create for Smart4Fabry disease.

Quality control

Achieve quality control over the self-assembly of nano-GLA molecular components and its physicochemical parameters.


Develop a nano-GLA capable of crossing the BBB.


Construction of a GMP plant for the production of the quantities of the nanoformulation needed for regulatory pre-clinical and future clinical trials.


Development of the GLA nanoformulation following the requirements of the pharmaceutical industry and regulatory authorities.


Create a realistic exploitation plan and business model, based on experience from the companies in the rare diseases market, in order to ensure the translation of the project results to patients suffering from Fabry disease.